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ᣂක⮎ຠߩ㐿⊒ᦼ㑆㧔ೋ࿁ᴦ㛎⸘↹ዯឭ಴ᣣ㨪ᛚ⹺ᣣ㧕

7┨ 㐿⊒ᦼ㑆ߣ㑐ଥߔࠆ࿃ሶ

࿑ 34 㐿⊒ᦼ㑆ߩផ⒖㧔ਛᄩ୯㧕㧔⛯߈㧕

82.4 24.8

88.1 16.0

27.6 15.6

35.9 18.6

41.5 17.2

35.7 22.3

54.1 21.3

42.3 19.6

32.1 18.4

0204060801001st CTPN to Approval (months)

2000 2001 2002 2003 2004 2005 2006 2007 2008 1st CTPN to NDA NDA to Approval

ೋ࿁ᴦ㛎⸘↹ዯ䌾↳⺧ ᛚ⹺↳⺧䌾ᛚ⹺ 䋨ᛚ⹺ᐕ䋩

⊒ᦼ㑆䋨᦬ᢙ䋩

NMEએᄖ

ᵈ㧦⥃ᐥ㐿⊒ᦼ㑆㧔NME 187 ຠ⋡ޔNME એᄖ

155

ຠ⋡㧕 ޔክᩏᦼ㑆㧔NME 230 ຠ⋡ޔ

NME

એᄖ

256

ຠ⋡㧕߇ߘࠇߙࠇ▚಴ߢ߈ߚᛚ⹺ຠ⋡ࠍኻ⽎ߣߒߚ

⴫ 33 㐿⊒ᦼ㑆ߩផ⒖

⥃ᐥ㐿⊒ᦼ㑆 ክᩏᦼ㑆 㐿⊒ᦼ㑆

ᛚ⹺ᐕ N ਛᄩ୯ ᐔဋ୯ SD N ਛᄩ୯ ᐔဋ୯ SD N ਛᄩ୯ ᐔဋ୯ SD

ో૕

2000 43 79.6 77.9 34.6 67 28.3 31.9 20.1 43 113.7 110.5 39.1 2001 24 74.5 77.3 32.0 39 16.8 26.1 21.4 24 97.3 99.2 38.1 2002 26 64.1 62.3 30.9 43 17.7 25.2 19.0 26 83.4 87.0 39.2 2003 24 56.0 62.2 34.9 29 19.1 23.2 17.3 24 73.2 86.9 43.2 2004 17 63.6 64.3 30.8 28 18.3 19.4 18.2 17 81.0 88.3 32.0 2005 34 54.2 65.8 42.7 47 24.0 25.4 13.1 34 87.0 93.2 48.2 2006 51 60.9 70.6 53.9 72 22.8 29.1 20.1 51 87.1 100.0 57.7 2007 63 52.4 59.0 36.2 83 20.0 25.1 20.7 63 76.2 85.3 42.4 2008 60 44.6 66.6 52.7 78 19.0 20.0 11.0 60 67.3 88.3 57.4 ว⸘ 342 59.5 67.1 42.1 486 20.6 25.5 18.4 342 85.5 93.3 47.5 NME

2000 33 79.6 78.3 29.2 40 31.8 34.5 22.2 33 115.8 113.1 32.9 2001 17 66.9 69.7 29.8 22 18.5 25.0 18.6 17 93.4 92.9 38.8 2002 22 66.8 68.2 29.9 24 21.0 29.1 22.1 22 94.4 94.8 37.5 2003 14 68.8 67.7 18.8 15 20.5 23.1 14.9 14 87.2 92.4 29.8 2004 11 88.8 74.9 32.1 16 19.9 22.1 23.4 11 115.7 102.6 29.7 2005 16 69.2 71.6 36.0 21 25.0 26.9 15.6 16 99.7 102.6 36.1 2006 19 66.1 75.0 50.0 23 25.1 36.3 28.5 19 94.8 109.4 58.2 2007 28 61.3 70.5 40.5 35 21.4 30.2 28.1 28 92.2 102.7 49.8 2008 27 78.4 91.4 57.1 34 19.1 21.3 13.2 27 104.3 115.5 62.2 ว⸘ 187 70.8 75.1 38.7 230 21.9 28.3 22.0 187 102.4 104.4 44.6 NMEએᄖ

2000 10 82.4 76.7 50.6 27 24.8 27.9 15.9 10 95.2 102.2 56.4 2001 7 88.1 95.9 31.5 17 16.0 27.5 25.1 7 102.7 114.5 34.1 2002 4 27.6 29.5 6.0 19 15.6 20.3 13.2 4 41.9 44.0 5.8 2003 10 35.9 54.4 49.9 14 18.6 23.2 20.1 10 57.0 79.1 58.0 2004 6 41.5 44.7 16.1 12 17.2 15.8 6.6 6 61.8 61.9 14.6 2005 18 35.7 60.7 48.3 26 22.3 24.2 10.9 18 53.6 84.8 56.7 2006 32 54.1 68.0 56.6 49 21.3 25.7 13.7 32 79.5 94.5 57.5 2007 35 42.3 49.7 29.9 48 19.6 21.4 11.9 35 63.8 71.4 29.2 2008 33 32.1 46.4 39.1 44 18.4 18.9 8.9 33 52.4 66.1 42.5 ว⸘ 155 40.0 57.5 44.1 256 19.4 22.9 14.1 155 63.8 80.0 47.5

ᵈ㧦⥃ᐥ㐿⊒ᦼ㑆ޔክᩏᦼ㑆ޔ㐿⊒ᦼ㑆߇ߘࠇߙࠇ▚಴ߢ߈ߚᛚ⹺ຠ⋡ࠍኻ⽎ߣߒߚ

7.2. ⥃ᐥ㐿⊒ᦼ㑆ޔክᩏᦼ㑆ޔ㐿⊒ᦼ㑆ߦᓇ㗀ࠍਈ߃ࠆ࿃ሶ

⥃ᐥ㐿⊒ᦼ㑆ޔክᩏᦼ㑆߅ࠃ߮㐿⊒ᦼ㑆ߩ㐳ߐߦᓇ㗀ࠍਈ߃ࠆ࿃ሶࠍ࿁Ꮻಽᨆߦߡᬌ⸛ߒߚޕ3ߟߩ ᦼ㑆ߩ㐳ߐࠍߘࠇߙࠇⵍ⺑᣿ᄌᢙޔࠕࡦࠤ࡯࠻⺞ᩏߦߡ࠺࡯࠲ࠍ෼㓸ߒߚᛚ⹺ຠ⋡ޔ↳⺧ડᬺޔ⥃ᐥ㐿

⊒߅ࠃ߮ᛚ⹺ክᩏߦ㑐ࠊࠆ࿃ሶ㧔⴫ 34㧕ࠍ⺑᣿ᄌᢙߣߒޔⶄᢙߩ࿃ሶߩᓇ㗀ࠍหᤨߦ⺞ᢛߒߚ਄ߢޔ ฦᦼ㑆ߦ᦭ᗧߥᓇ㗀ࠍਈ߃ࠆ․ᕈࠍᦨዊੑਸ਼ᴺߦߡផ⸘ߒߚޕ

⴫ 34 ࿁Ꮻಽᨆߦ↪޿ߚ⺑᣿ᄌᢙ

ಽ㘃 ⺑᣿ᄌᢙ

ຠ⋡ ↳⺧඙ಽ㧔NME/NMEએᄖ㧕

⮎ലಽ㘃

ൻቇวᚑຠ/ࡃࠗࠝ࠹ࠢࡁࡠࠫ࡯ᔕ↪ක⮎ຠ

ห⒳หല⮎ߩ᦭ή

↳⺧ડᬺ ડᬺ࿖☋㧔࿖ౝ/ᄖ࿖㧕

⥄␠㐿⊒ຠ/ઁ␠ዉ౉ຠ

ᒰ⹥∔ᖚ㗔ၞߦ߅ߌࠆ㐿⊒⚻㛎ߩ᦭ή

⥃ᐥ㐿⊒ ╙Τ⋧⹜㛎⚳ੌᓟ⋧⺣ታᣉߩ᦭ή

↳⺧೨⋧⺣ታᣉߩ᦭ή

ᛚ⹺ክᩏ PMDA⸳┙೨ᓟߩ↳⺧

ክᩏ඙ಽ㧔ㅢᏱክᩏ/ఝవክᩏ㧕

⹏ଔ⾗ᢱߣߒߚ⥃ᐥ⹜㛎ᢙ ᄖ࿖⥃ᐥ࠺࡯࠲ߩ೑↪

ቇળ࡮ᖚ⠪࿅૕ߩⷐᦸᦠߩ᦭ή ᛚ⹺᧦ઙߩ᦭ή

7.2.1. ࿖ౝ⥃ᐥ⹜㛎ࠍታᣉߒߚᣂක⮎ຠߩ㐿⊒ᦼ㑆

ߪߓ߼ߦޔ2000㨪2008ᐕߦᛚ⹺ߐࠇߚ486ຠ⋡ߩ߁ߜޔ࿖ౝߢ⥃ᐥ⹜㛎߇ታᣉߐࠇޔ⥃ᐥ㐿⊒ᦼ㑆߅ ࠃ߮ክᩏᦼ㑆ߩਔᣇ߇▚಴น⢻ߢޔ⴫ 34ߦ␜ߒߚ⺑᣿ᄌᢙߩ࠺࡯࠲߇ᓧࠄࠇߚᣂක⮎ຠ306ຠ⋡

㧔63.0%㧕ࠍኻ⽎ߣߒߚޕⵍ⺑᣿ᄌᢙ߅ࠃ߮⺑᣿ᄌᢙߩၮᧄ⛔⸘㊂ࠍ⴫ 35ߦ␜ߒߚޕⵍ⺑᣿ᄌᢙߢ޽ࠆ

⥃ᐥ㐿⊒ᦼ㑆ޔክᩏᦼ㑆ޔ㐿⊒ᦼ㑆ߩᐔဋ୯rSDߪ67.9r42.7ࡨ᦬ޔ26.8r18.5ࡨ᦬ޔ94.6r47.4ࡨ᦬

ߢ޽ࠅ㧔⴫ 35㧕ޔ╙4┨ߦߡ⥃ᐥ㐿⊒ᦼ㑆ࠍ⸃ᨆߒߚ342ຠ⋡㧔67.1r42.1ࡨ᦬ޔ⴫ 41㧕ޔ╙5┨ߦߡ

⴫ 35 ⵍ⺑᣿ᄌᢙޔ⺑᣿ᄌᢙߩၮᧄ⛔⸘㊂㧔࿖ౝ⥃ᐥ⹜㛎޽ࠅߩᣂක⮎ຠ㧕

ᄌᢙ ᐔဋ୯ SD ᦨዊ ᦨᄢ

ⵍ⺑᣿ᄌᢙ

⥃ᐥ㐿⊒ᦼ㑆䋨᦬ᢙ䋩 67.9 42.7 0.9 228.8 ክᩏᦼ㑆䋨᦬ᢙ䋩 26.8 18.5 1.4 135.4 㐿⊒ᦼ㑆䋨᦬ᢙ䋩 94.6 47.7 10.3 253.5

⺑᣿ᄌᢙ*1

ᣂ᦭ലᚑಽ฽᦭ක⮎ຠ㧔NME㧕એᄖ 0.46 0.50 0 1

ࡃࠗࠝක⮎ຠ 0.14 0.34 0 1

ห⒳หല⮎޽ࠅ 0.73 0.45 0 1

ዉ౉ຠ 0.28 0.45 0 1

╙2⋧⚳ੌᓟ⋧⺣ࠍታᣉ 0.38 0.49 0 1

↳⺧೨⋧⺣ࠍታᣉ 0.46 0.50 0 1

2004ᐕ4᦬㧔PMDA⸳┙㧕એ㒠ߩ↳⺧ 0.45 0.50 0 1

ఝవክᩏ 0.23 0.42 0 1

⮎ലಽ㘃 N (%)

ਛᨔ␹⚻ 21 (6.9)

⸃ᾲ㎾∩ᶖἻ 2 (0.7)

ᧃ᪳␹⚻ 5 (1.6)

⌒⑼࡮⡊㥦⑼ 14 (4.6)

᛫ࠕ࡟࡞ࠡ࡯ 11 (3.6)

ᓴⅣེ 29 (9.5)

๭ๆེ 6 (2.0)

ᶖൻེ 11 (3.6)

ᶖൻᕈẩ≌ 4 (1.3) ࡎ࡞ࡕࡦ೷ 21 (6.9) ᴲዩ↢ᱺེ 8 (2.6)

ᄖ⊹↪ 8 (2.6)

ઍ⻢ᕈ 47 (15.4)

᛫ᖡᕈ⣲≌ 35 (11.4)

᡼኿ᕈක⮎ຠ 3 (1.0)

ክᩏᦼ㑆ࠍ⸃ᨆߒߚ486ຠ⋡㧔25.5r18.4ࡨ᦬ޔ⴫ 11㧕ޔ7.1㗄ߦߡ㐿⊒ᦼ㑆ࠍ⸃ᨆߒߚ342ຠ⋡㧔93.3 r47.5ࡨ᦬ޔ⴫ 33㧕ߣߘࠇߙࠇ㘃ૃߒߡ߅ࠅޔ⸃ᨆኻ⽎ߦࠃࠆ㆑޿ߪ⹺߼ࠄࠇߥ߆ߞߚޕ

⺑᣿ᄌᢙߪޔ⹏ଔ⾗ᢱߣߒߚ⥃ᐥ⹜㛎ᢙ߅ࠃ߮⮎ലಽ㘃એᄖߪޔޟ⹥ᒰߖߕ/⹥ᒰߔࠆޔߥߒ/޽ࠅޠߩ 2୯ߩ࠳ࡒ࡯ᄌᢙߢ޽ࠅޔ⴫ 35ߩ୯ߪ⸃ᨆኻ⽎ߦ߅ߌࠆഀวࠍ0㨪1ߩ▸࿐ߢ␜ߒߡ޿ࠆޕߔߥࠊߜޔ

46%ߩຠ⋡߇NMEએᄖߢ޽ࠅޔ46%߇↳⺧೨ߦᴦ㛎⋧⺣ࠍታᣉޔ45%߇2004ᐕ4᦬એ㒠ߦPMDAߦ↳

⺧ߐࠇߚຠ⋡ޔ23%߇ఝవክᩏຠ⋡ޔ36%߇ᄖ࿖Phase 2㨪3⹜㛎࠺࡯࠲ࠍ೑↪ޔ53%߇ᄖ⾗♽ડᬺ*2ߦ ࠃࠆ↳⺧ߢ޽ߞߚޕ⹏ଔ⾗ᢱߣߒߚ⥃ᐥ⹜㛎ᢙߩᐔဋ୯ߪ11.40ߢ޽ࠅޔ1㨪93⹜㛎ߩ▸࿐ߦ޽ߞߚޕ

⮎ലಽ㘃ߪߎࠇ߹ߢߣห᭽ߦޔ⮎ോ౏ႎ╬ߢ↪޿ࠄࠇߡ޿ࠆ21ಽ㘃ࠍ↪޿ߡ⺞ᢛߒߚޕ

࿑ 35ޔ⴫ 36ߪ࿁Ꮻಽᨆߩ⚿ᨐࠍ␜ߒߚ߽ߩߢ޽ࠆޕ࿑ 35ߪᏀ߆ࠄ㗅ߦ⥃ᐥ㐿⊒ᦼ㑆ޔክᩏᦼ㑆ޔ 㐿⊒ᦼ㑆ߩ⚿ᨐࠍ⴫ߒߡ߅ࠅޔ࿁Ꮻଥᢙߩ୯ࠍ᫔ࠣ࡜ࡈߢ␜ߒߡ޿ࠆޕ࿁Ꮻଥᢙ߇ᱜߢ޽ࠇ߫ฦᦼ㑆ߪ 㐳ߊޔ⽶ߢ޽ࠇ߫⍴ߊߥߞߡ߅ࠅޔ୯߇ᄢ߈޿߶ߤߘߩᓇ㗀߇ᄢ߈޿ߎߣࠍ⴫ߒߡ޿ࠆޕ߹ߚޔߘߩᓇ 㗀߇⛔⸘⊛ߦ᦭ᗧߥ⺑᣿ᄌᢙߦߪࠕࠬ࠹࡝ࠬࠢޟ*ޠࠍઃߒߚ㧔᦭ᗧ᳓Ḱ㧦* p <0.1, ** p <0.05, *** p <0.01㧕ޕ

ᧄ⚿ᨐ߆ࠄޔઁߩ᧦ઙ߇หߓߢ޽ࠇ߫ޔNMEߣᲧߴߡNMEએᄖߩຠ⋡ߩ⥃ᐥ㐿⊒ᦼ㑆ߪ᦭ᗧߦ⍴޿

ߎߣ߇␜ߐࠇߚޕห᭽ߦޔᛚ⹺᧦ઙ޽ࠅߩຠ⋡ޔᄖ࿖Phase 2㨪3⹜㛎࠺࡯࠲ࠍ೑↪ߒߚຠ⋡ߩ⥃ᐥ㐿⊒

ᦼ㑆߽᦭ᗧߦ⍴߆ߞߚޕ৻ᣇޔᛚ⹺ຠ⋡ߣหߓ∔ᖚ㗔ၞߢ㐿⊒⚻㛎߇޽ࠆ႐วߪޔ੍ᗐߦ෻ߒߡ⥃ᐥ㐿

⊒ᦼ㑆߇᦭ᗧߦ㐳޿ߣ޿߁⚿ᨐ߇ᓧࠄࠇߚޕ↳⺧೨⋧⺣ࠍታᣉߒߚ႐วޔክᩏᦼ㑆߇᦭ᗧߦ⍴߆ߞߚ෻

㕙ޔ⥃ᐥ㐿⊒ᦼ㑆߇᦭ᗧߦ㐳ߊޔ2ߟࠍวࠊߖߚ㐿⊒ᦼ㑆ߢߪਔ⠪ߩᓇ㗀߇⋧Ვߐࠇߡᓇ㗀ߪ⹺߼ࠄࠇ ߥ߆ߞߚޕ߹ߚޔPMDA⸳┙ᓟߩ↳⺧ຠ⋡ޔఝవክᩏຠ⋡ߩክᩏᦼ㑆߽᦭ᗧߦ⍴޿ߎߣࠍ␜ໂߐࠇߚޕ NMEએᄖߩຠ⋡ޔPMDA⸳┙ᓟߩ↳⺧ޔఝవክᩏޔᛚ⹺᧦ઙ޽ࠅޔᄖ࿖⥃ᐥ࠺࡯࠲ߩ೑↪ߪޔߘࠇߙ ࠇ⥃ᐥ㐿⊒ᦼ㑆߅ࠃ߮ክᩏᦼ㑆ߢ␜ߐࠇߚ᦭ᗧߥᓇ㗀߇㐿⊒ᦼ㑆ߢ߽⹺߼ࠄࠇߚޕ

࿑ 35 㐿⊒ᦼ㑆ߦᓇ㗀ࠍਈ߃ࠆ࿃ሶ㧔࿖ౝ⥃ᐥ⹜㛎޽ࠅߩᣂක⮎ຠ㧕

-7.1

8.9 -9.9

0.2 -13.1

4.5 -8.8

-6.9

11.1 4.3 -6.9

2.9 4.9 -20.6

-20 -10 0 10

-0.7 -2.6 -2.9

0.1 -2.2

0.8 -9.2

-7.6 -6.6

-2.0 2.1 -1.0

1.7 -2.8

-10 0 10

-7.9

6.3 -12.9

0.3 -15.3

5.3 -18.0

-14.5

4.5 2.3 -4.9

1.9 6.7 -23.5

-20 -10 0 10

࿁Ꮻଥᢙ NMEએᄖ

ห⒳หല⮎䈅䉍 ዉ౉ຠ

ᄖ⾗♽ડᬺ

╙2⋧⚳ੌᓟ⋧⺣

↳⺧೨⋧⺣

PMDA⸳┙ᓟ䈱↳⺧

ఝవክᩏ ቇળ䊶ᖚ⠪ⷐᦸᦠ ᛚ⹺᧦ઙ䈅䉍 P1䌾3⹜㛎ᢙ ᄖ࿖P2䌾3⹜㛎೑↪

㐿⊒⚻㛎䈅䉍 䊋䉟䉥ක⮎ຠ

***

**

***

***

**

*** ***

** **

**

***

⥃ᐥ㐿⊒ᦼ㑆 ክᩏᦼ㑆 㐿⊒ᦼ㑆

*

*

ᵈ㧦᦭ᗧ᳓Ḱ㧦* p <0.1, ** p <0.05, *** p <0.01㧧⮎ലಽ㘃ߪ⋭⇛ߒߚ

⴫ 36 㐿⊒ᦼ㑆ߦᓇ㗀ࠍਈ߃ࠆ࿃ሶ㧔࿖ౝ⥃ᐥ⹜㛎޽ࠅߩᣂක⮎ຠ㧕

⥃ᐥ㐿⊒ᦼ㑆 ክᩏᦼ㑆 㐿⊒ᦼ㑆

⺑᣿ᄌᢙ ଥᢙ SE p୯ ଥᢙ SE p୯ ଥᢙ SE p୯ ᣂ᦭ലᚑಽ฽᦭ක⮎ຠ㧔NME㧕એᄖ -20.6 5.8 0.000 *** -2.8 2.4 0.239 -23.5 6.2 0.000 ***

ࡃࠗࠝක⮎ຠ 4.9 7.8 0.529 1.7 3.2 0.588 6.7 8.4 0.429 ห⒳หല⮎䈅䉍 2.9 5.5 0.604 -1.0 2.3 0.657 1.9 6.0 0.755

ዉ౉ຠ -6.9 5.5 0.210 2.1 2.3 0.363 -4.9 6.0 0.414

╙2⋧⚳ੌᓟ⋧⺣䉕ታᣉ 4.3 5.1 0.398 -2.0 2.1 0.336 2.3 5.5 0.676

↳⺧೨⋧⺣ࠍታᣉ 11.1 4.9 0.024 ** -6.6 2.0 0.001 *** 4.5 5.3 0.388

2004ᐕ4᦬䋨PMDA⸳┙䋩એ㒠䈱↳⺧ -6.9 5.1 0.180 -7.6 2.1 0.000 *** -14.5 5.5 0.009 ***

ఝవክᩏ -8.8 7.0 0.211 -9.2 2.9 0.002 *** -18.0 7.6 0.018 **

ቇળ䊶ᖚ⠪࿅૕䈱ⷐᦸᦠ䈅䉍 4.5 5.4 0.410 0.8 2.2 0.724 5.3 5.9 0.369 ᛚ⹺᧦ઙ䈅䉍 -13.1 5.8 0.023 ** -2.2 2.4 0.356 -15.3 6.2 0.014 **

⹏ଔ⾗ᢱ䈫䈚䈢P1䌾3⹜㛎䈱ᢙ 0.2 0.2 0.308 0.1 0.1 0.230 0.3 0.2 0.161 ᄖ࿖P2䌾3⹜㛎䉕೑↪ -9.9 5.1 0.055 * -2.9 2.1 0.167 -12.9 5.5 0.021 **

ᒰ⹥∔ᖚ㗔ၞ䈱㐿⊒⚻㛎䈅䉍 8.9 5.0 0.074 * -2.6 2.0 0.196 6.3 5.4 0.242 ᄖ⾗♽ડᬺ -7.1 5.4 0.190 -0.7 2.2 0.740 -7.9 5.8 0.179

⮎ലಽ㘃䋨ෳᾖ䉦䊁䉯䊥䊷䋺ਛᨔ␹⚻䋩

⸃ᾲ㎾∩ᶖἻ -15.5 28.3 0.584 -0.2 11.6 0.983 -15.7 30.5 0.606

ᧃ᪳␹⚻ 9.5 19.5 0.625 -9.2 8.0 0.253 0.4 21.0 0.986

⌒⑼࡮⡊㥦⑼ -27.3 13.4 0.042 ** -7.2 5.5 0.193 -34.5 14.4 0.018 **

᛫ࠕ࡟࡞ࠡ࡯ -33.9 14.5 0.020 ** -9.8 5.9 0.098 * -43.7 15.6 0.005 ***

ᓴⅣེ -10.0 11.1 0.369 -8.7 4.6 0.057 * -18.7 12.0 0.119

๭ๆེ -36.7 17.9 0.042 ** -9.3 7.4 0.205 -46.0 19.3 0.018 **

ᶖൻེ -31.7 14.9 0.034 ** -10.5 6.1 0.086 * -42.3 16.0 0.009 ***

ᶖൻᕈẩ≌ 74.8 21.3 0.001 *** -4.8 8.7 0.587 70.1 22.9 0.002 ***

ࡎ࡞ࡕࡦ೷ -13.9 12.6 0.271 -4.3 5.2 0.410 -18.1 13.5 0.182 ᴲዩ↢ᱺེ -32.6 16.1 0.044 ** -8.5 6.6 0.200 -41.1 17.3 0.018 **

ᄖ⊹↪ -29.3 16.1 0.071 * -4.9 6.6 0.458 -34.2 17.4 0.050 *

ઍ⻢ᕈ -21.3 10.5 0.042 ** -9.3 4.3 0.032 ** -30.6 11.3 0.007 ***

᛫ᖡᕈ⣲≌ -23.3 11.4 0.042 ** -9.1 4.7 0.053 * -32.3 12.3 0.009 ***

᡼኿ᕈක⮎ຠ -50.5 24.8 0.042 ** 60.4 10.2 0.000 *** 9.9 26.7 0.712

᛫↢‛⾰ -28.7 13.9 0.040 ** -12.2 5.7 0.033 ** -40.9 15.0 0.007 ***

ൻቇ≮ᴺ೷ -24.5 11.4 0.033 ** -11.9 4.7 0.012 ** -36.3 12.3 0.003 ***

↢‛ቇ⊛⵾೷ -25.3 13.4 0.061 * -5.3 5.5 0.334 -30.6 14.5 0.036 **

㚟⯻⮎ -49.0 39.8 0.219 -17.3 16.3 0.291 -66.3 42.8 0.123

ㅧᓇ೷࡮⸻ᢿ⮎ -30.8 15.3 0.045 ** -6.3 6.3 0.313 -37.2 16.5 0.025 **

ߘߩઁ -43.8 14.0 0.002 *** -9.3 5.7 0.106 -53.1 15.1 0.001 ***

Eଥᢙ 99.6 11.0 0.000 *** 46.7 4.5 0.000 *** 146.3 11.9 0.000 ***

Nᢙ 306 306 306

p୯ 0.000 0.000 0.000

⥄↱ᐲୃᱜᷣ䉂᳿ቯଥᢙ 0.226 0.304 0.280

ᵈ㧦᦭ᗧ᳓Ḱ㧦* p <0.1, ** p <0.05, *** p <0.01

7.2.2. ࿖ౝ⥃ᐥ⹜㛎ߩ᦭ήࠍ໧ࠊߥ޿ᣂක⮎ຠߩክᩏᦼ㑆

ᰴߦޔ࿖ౝߢ⥃ᐥ⹜㛎ࠍታᣉߖߕߦᛚ⹺ߐࠇߚ․଀⊛ߥᣂ⮎ࠍ฽߻397ຠ⋡ࠍኻ⽎ߦޔክᩏᦼ㑆ߣ㑐 ଥߔࠆ࿃ሶࠍ⸃ᨆߒߚޕⵍ⺑᣿ᄌᢙ߅ࠃ߮⺑᣿ᄌᢙߩၮᧄ⛔⸘㊂ࠍ⴫ 37ޔ࿁Ꮻಽᨆߩ⚿ᨐࠍ࿑ 36߅ࠃ

߮⴫ 38ߦ␜ߒߚޕክᩏᦼ㑆ߩᐔဋ୯rSDߪ26.2r18.9ࡨ᦬ߢ޽ࠅޔ7.2.1㗄ߩ࿖ౝ⥃ᐥ⹜㛎޽ࠅߩᣂ ක⮎ຠߣห᭽ߢ޽ߞߚ㧔26.8r18.5ࡨ᦬ޔ⴫ 35㧕ޕ৻ᣇޔ࿖ౝߢ⥃ᐥ⹜㛎ࠍታᣉߒߡ޿ߥ޿ຠ⋡߇฽߹

ࠇߡ޿ࠆߚ߼ޔ࿖ౝ⥃ᐥ⹜㛎޽ࠅߩ⸃ᨆኻ⽎ߦᲧߴޔNMEએᄖߩຠ⋡ޔఝవክᩏຠ⋡ޔᛚ⹺᧦ઙ޽ࠅ

ߣ޿߁⚿ᨐ߇ᓧࠄࠇߚޕ৻ᣇߢޔߘߩᓇ㗀ߪዊߐ޿ߥ߇ࠄޔ⹏ଔ⾗ᢱߣߒߚ࿖ౝᄖߩPhase 1㨪3⹜㛎ᢙ ߇ᄙ޿߶ߤክᩏᦼ㑆߇᦭ᗧߦ㐳޿ߎߣ߇␜ໂߐࠇߚޕ

⴫ 37 ⵍ⺑᣿ᄌᢙޔ⺑᣿ᄌᢙߩၮᧄ⛔⸘㊂㧔࿖ౝ⥃ᐥ⹜㛎ߩ᦭ήࠍ໧ࠊߥ޿ᣂක⮎ຠ㧕

ᄌᢙ ᐔဋ୯ SD ᦨዊ ᦨᄢ

ⵍ⺑᣿ᄌᢙ

ክᩏᦼ㑆䋨᦬ᢙ䋩 26.2 18.9 1.4 135.4

⺑᣿ᄌᢙ*1

ᣂ᦭ലᚑಽ฽᦭ක⮎ຠ㧔NME㧕એᄖ 0.53 0.50 0 1

ࡃࠗࠝක⮎ຠ 0.13 0.34 0 1

ห⒳หല⮎޽ࠅ 0.71 0.46 0 1

ዉ౉ຠ 0.27 0.45 0 1

╙2⋧⚳ੌᓟ⋧⺣ࠍታᣉ 0.30 0.46 0 1

↳⺧೨⋧⺣ࠍታᣉ 0.39 0.49 0 1

2004ᐕ4᦬㧔PMDA⸳┙㧕એ㒠ߩ↳⺧ 0.43 0.50 0 1

ఝవክᩏ 0.30 0.46 0 1

ቇળ࡮ᖚ⠪࿅૕ߩⷐᦸᦠ޽ࠅ 0.36 0.48 0 1

ᛚ⹺᧦ઙ޽ࠅ 0.41 0.49 0 1

⹏ଔ⾗ᢱߣߒߚP1㨪3⹜㛎ߩᢙ 10.68 12.93 0 93 ᄖ࿖P2㨪3⹜㛎ࠍ೑↪ 0.37 0.48 0 1 ᒰ⹥∔ᖚ㗔ၞߩ㐿⊒⚻㛎޽ࠅ 0.51 0.50 0 1

ᄖ⾗♽ડᬺ 0.53 0.50 0 1

Nᢙ*2 397

⮎ലಽ㘃 N (%)

ਛᨔ␹⚻ 23 (5.8)

⸃ᾲ㎾∩ᶖἻ 3 (0.8)

ᧃ᪳␹⚻ 6 (1.5)

⌒⑼࡮⡊㥦⑼ 18 (4.5)

᛫ࠕ࡟࡞ࠡ࡯ 12 (3.0)

ᓴⅣེ 35 (8.8)

๭ๆེ 8 (2.0)

ᶖൻེ 12 (3.0)

ᶖൻᕈẩ≌ 9 (2.3) ࡎ࡞ࡕࡦ೷ 29 (7.3) ᴲዩ↢ᱺེ 9 (2.3)

ᄖ⊹↪ 10 (2.5)

ઍ⻢ᕈ 68 (17.1)

᛫ᖡᕈ⣲≌ 41 (10.3)

᡼኿ᕈක⮎ຠ 3 (0.8)

᛫↢‛⾰ 21 (5.3)

ൻቇ≮ᴺ೷ 42 (10.6)

↢‛ቇ⊛⵾೷ 23 (5.8)

㚟⯻⮎ 1 (0.3)

ㅧᓇ೷࡮⸻ᢿ⮎ 10 (2.5)

ߘߩઁ 14 (3.5)

ว⸘ 397 (100.0)

*1 0=ޟ⹥ᒰߖߕޠ

ޔ ޟߥߒޠ, 1=ޟ⹥ᒰߔࠆޠ ޔ ޟ޽ࠅޠ

*2

ክᩏᦼ㑆߅ࠃ߮ㆬᛯߒߚ⺑᣿ᄌᢙ߇ᓧࠄࠇߚຠ⋡ࠍኻ⽎ߣߒߚ

࿑ 36 ክᩏᦼ㑆ߦᓇ㗀ࠍਈ߃ࠆ࿃ሶ㧔࿖ౝ⥃ᐥ⹜㛎ߩ᦭ήࠍ໧ࠊߥ޿ᣂක⮎ຠ㧕

-0.1 -3.7

-5.0

0.1 -3.8

0.8 -7.8

-9.1

-6.1

-1.3

1.4 -1.9

1.7 -2.2

-10 0

࿁Ꮻଥᢙ NMEએᄖ

ห⒳หല⮎䈅䉍 ዉ౉ຠ

ᄖ⾗♽ડᬺ

╙2⋧⚳ੌᓟ⋧⺣

↳⺧೨⋧⺣

PMDA⸳┙ᓟ䈱↳⺧

ఝవክᩏ ቇળ䊶ᖚ⠪ⷐᦸᦠ ᛚ⹺᧦ઙ䈅䉍 P1䌾3⹜㛎ᢙ ᄖ࿖P2䌾3⹜㛎೑↪

㐿⊒⚻㛎䈅䉍 䊋䉟䉥ක⮎ຠ

**

**

**

**

*

ክᩏᦼ㑆

ᵈ㧦᦭ᗧ᳓Ḱ㧦* p <0.1, ** p <0.05, *** p <0.01㧧⮎ലಽ㘃ߪ⋭⇛ߒߚ

⴫ 38 ክᩏᦼ㑆ߦᓇ㗀ࠍਈ߃ࠆ࿃ሶ㧔࿖ౝ⥃ᐥ⹜㛎ߩ᦭ήࠍ໧ࠊߥ޿ᣂක⮎ຠ㧕

⺑᣿ᄌᢙ ଥᢙ SE p୯ ᣂ᦭ലᚑಽ฽᦭ක⮎ຠ㧔NME㧕એᄖ -2.2 2.0 0.261 ࡃࠗࠝක⮎ຠ 1.7 2.8 0.545 ห⒳หല⮎޽ࠅ -1.9 1.9 0.321 ዉ౉ຠ 1.4 2.0 0.471

╙2⋧⚳ੌᓟ⋧⺣ࠍታᣉ -1.3 1.9 0.514

↳⺧೨⋧⺣ࠍታᣉ -6.1 1.8 0.001 ***

2004ᐕ4᦬㧔PMDA⸳┙㧕એ㒠ߩ↳⺧ -9.1 1.8 0.000 ***

ఝవክᩏ -7.8 2.3 0.001 ***

ቇળ࡮ᖚ⠪࿅૕ߩⷐᦸᦠ޽ࠅ 0.8 1.9 0.656 ᛚ⹺᧦ઙ޽ࠅ -3.8 2.0 0.055 *

⹏ଔ⾗ᢱߣߒߚP1㨪3⹜㛎ߩᢙ 0.1 0.1 0.061 * ᄖ࿖P2㨪3⹜㛎ࠍ೑↪ -5.0 1.8 0.006 ***

ᒰ⹥∔ᖚ㗔ၞߩ㐿⊒⚻㛎޽ࠅ -3.7 1.7 0.033 **

ᄖ⾗♽ડᬺ -0.1 1.9 0.956

⮎ലಽ㘃䋨ෳᾖ䉦䊁䉯䊥䊷䋺ਛᨔ␹⚻䋩

⸃ᾲ㎾∩ᶖἻ 2.7 9.6 0.781

ᧃ᪳␹⚻ -9.2 7.3 0.206

⌒⑼࡮⡊㥦⑼ -2.7 5.0 0.587

᛫ࠕ࡟࡞ࠡ࡯ -7.2 5.7 0.204

ᓴⅣེ -5.2 4.2 0.220

๭ๆེ 3.6 6.4 0.573

ᶖൻེ -9.7 5.8 0.093 *

ᶖൻᕈẩ≌ -5.9 6.3 0.348 ࡎ࡞ࡕࡦ೷ -3.9 4.6 0.401 ᴲዩ↢ᱺེ -5.9 6.2 0.345

ᄖ⊹↪ -4.5 6.0 0.453

ઍ⻢ᕈ -8.1 3.9 0.039 **

᛫ᖡᕈ⣲≌ -6.4 4.3 0.137

᡼኿ᕈක⮎ຠ 62.4 9.9 0.000 ***

᛫↢‛⾰ -11.0 4.8 0.024 **

ൻቇ≮ᴺ೷ -13.3 4.2 0.002 ***

↢‛ቇ⊛⵾೷ -3.5 5.1 0.497

㚟⯻⮎ -16.9 16.1 0.294

ㅧᓇ೷࡮⸻ᢿ⮎ -7.1 5.9 0.233

ߘߩઁ -6.9 5.4 0.202

Eଥᢙ 46.6 4.1 0.000 ***

Nᢙ 397

p୯ 0.000

⥄↱ᐲୃᱜᷣ䉂᳿ቯଥᢙ 0.338

ᵈ㧦᦭ᗧ᳓Ḱ㧦* p <0.1, ** p <0.05, *** p <0.01

࿁Ꮻಽᨆߦ⚵ߺ౉ࠇߚ⺑᣿ᄌᢙߩ߁ߜޔNMEએᄖߩຠ⋡ޔPMDA⸳┙ᓟߩ↳⺧ߣ޿ߞߚ߽ߩߪᚲਈ ߩ․ᕈߢ޽ࠆޕ৻ᣇޔ↳⺧೨⋧⺣ߩታᣉޔᄖ࿖⥃ᐥ࠺࡯࠲ߩ೑↪ޔㆊ෰ߩ㐿⊒⚻㛎ߣ޿ߞߚ߽ߩߪડᬺ

ߩ㐿⊒ᚢ⇛ߦ㑐ࠊࠆ࿃ሶߢ޽ࠅޔᚢ⇛ᰴ╙ߢᄌࠊࠅᓧࠆ߽ߩߢ޽ࠆޕߒߚ߇ߞߡޔ⥃ᐥ㐿⊒ߩല₸ൻ߿

ክᩏᦼ㑆ߩ⍴❗ࠍᬌ⸛ߔࠆ਄ߢޔߎࠇࠄߩ⚿ᨐߪෳ⠨ߦߥࠆߣ⠨߃ࠄࠇࠆޕ߹ߚޔఝవክᩏຠ⋡߿ᛚ⹺

᧦ઙ޽ࠅߩຠ⋡ߦ㑐ߒߡ߽ޔߘࠇߙࠇㅢᏱክᩏຠ⋡ޔᛚ⹺᧦ઙߥߒߩຠ⋡ߣߩ⋧㆑ޔ଀߃߫೨⠪ߢ޽ࠇ

߫ᓙߜᤨ㑆ߩᏅޔᓟ⠪ߢ޽ࠇ߫⥃ᐥ࠺࡯࠲ࡄ࠶ࠤ࡯ࠫߩࡏ࡝ࡘ࡯ࡓߩ㆑޿ߣ޿ߞߚὐ߇ᦼ㑆⍴❗ߦะߌ

8PMDAߣ↳⺧⠪ߩᛚ⹺ክᩏߦ㑐ߔࠆࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ

↳⺧ડᬺ߆ࠄߺߚPMDA߅ࠃ߮↳⺧ડᬺߩᛚ⹺ክᩏߦ㑐ߔࠆࡄࡈࠜ࡯ࡑࡦࠬࠍ⹏ଔߒߚޕ↳⺧ડᬺߪޔ ࠕࡦࠤ࡯࠻⺞ᩏታᣉᒰᤨߦ߅ߌࠆPMDA߅ࠃ߮↳⺧⠪⥄りߩࡄࡈࠜ࡯ࡑࡦࠬࠍ100ὐḩὐߢណὐߒߚޕ ᛚ⹺ክᩏߦ㑐ߔࠆࡄࡈࠜ࡯ࡑࡦࠬߦߪޔ↳⺧⾗ᢱߩክᩏ߿ᾖળ੐㗄ߩ߿ࠅߣࠅߦട߃ޔPMDAߢ޽ࠇ߫

ᴦ㛎⋧⺣߿ᴦ㛎⸘↹ዯ╬ߩኻᔕޔ↳⺧⠪ߢ޽ࠇ߫ᴦ㛎⋧⺣߿ᴦ㛎⸘↹ዯߩឭ಴⾗ᢱߩ⾰ޔⷙ೙ᒰዪߣߩ ኻᔕ╬ࠍ฽߼ߚޕ߹ߚޔ⺞ᩏIߦߡ࠺࡯࠲ࠍ෼㓸ߒߚᛚ⹺ຠ⋡ߦ㒢ࠄߕޔ⺞ᩏᒰᤨߦ↳⺧ડᬺ߇⚻㛎ߒ ߚઁߩຠ⋡ߦ߅ߌࠆᴦ㛎⋧⺣߿ᴦ㛎⸘↹ዯ╬ߩኻᔕ߽⹏ଔߩኻ⽎ߣߒߚޕᛚ⹺ຠ⋡߇ⶄᢙ޽ࠆ႐ว߽

1ડᬺ޽ߚࠅ1ߟߩ⹏ଔߣߒޔ౒ห㐿⊒ડᬺߦ߽⹏ଔࠍଐ㗬ߒߚޕ

↳⺧⠪ߦࠃࠆPMDAߩࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔࠍ࿑ 37ޔ↳⺧⠪⥄りߦኻߔࠆ⹏ଔࠍ࿑ 38ߦ4Ბ㓏⹏ଔ 㧔A㧦80㨪100ὐޔB㧦65㨪79ὐޔC㧦50㨪64ὐޔD㧦0㨪49ὐ㧕ߢ␜ߒߚޕ߹ߚޔὐᢙߩၮᧄ⛔⸘㊂ࠍ

⴫ 39ߦ␜ߒߚޕPMDAߦኻߔࠆ⹏ଔߪޔߎߩ3ᐕ㑆ߢA⹏ଔޔB⹏ଔߩഀว߇㘧べ⊛ߦჇടߒߡ߅ࠅޔ

↳⺧ડᬺ߇ᦨㄭߩPMDAߩࡄࡈࠜ࡯ࡑࡦࠬࠍ㜞ߊ⹏ଔߒߡ޿ࠆߎߣ߇ુ߃ࠆޕ↳⺧⠪⥄りߦኻߔࠆ⹏ଔ

⚿ᨐߪޔPMDAߦኻߔࠆ⹏ଔࠃࠅᏱߦ㜞ߊޔ2008ᐕߪA⹏ଔ߇31.0%ޔB⹏ଔ߇50.0%ߢ޽ߞߚޕክᩏ ㇱ೎ߩណὐ߽ⴕߞߚ2008ᐕᛚ⹺ຠ⋡ߢߪޔᒰᤨߩᣂ⮎ክᩏ╙৻ㇱ㧔╙1ಽ㊁ޔ╙4ಽ㊁ޔ᛫ᖡಽ㊁ޔ

ࠛࠗ࠭ක⮎ຠಽ㊁㧕߇ਛᄩ୯ޔᐔဋଔߣ߽ߦᦨ߽㜞߆ߞߚ߇ޔㇱ⟑㑆ߩᏅߪዊߐߊޔ᭎ߨห᭽ߩ୯ߢ޽

ߞߚ㧔࿑ 39ޔ⴫ 40㧕ޕ

࿑ 37 ᛚ⹺ክᩏߦ㑐ߔࠆPMDAߩࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ㧔2006㨪2008ᐕ㧕

18.6 60.5 18.6 2.3

4.4 35.6 57.8 2.2

2.6 23.7 65.8 7.9

0 20 40 60 80 100

% of PMDA's Grades 2008

2007 2006

A: 80-100 B: 65-79 C: 50-64 D: 0-49

䋨ᛚ⹺ᐕ䋩

PMDA䈱⹏ଔ䋨%䋩

࿑ 38 ᛚ⹺ክᩏߦ㑐ߔࠆ↳⺧⠪⥄りߩࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ㧔2006㨪2008ᐕ㧕

31.0 50.0 14.3 4.8

15.6 53.3 28.9 2.2

24.3 45.9 27.0 2.7

0 20 40 60 80 100

% of Applicant's Grades 2008

2007 2006

A: 80-100 B: 65-79 C: 50-64 D: 0-49

䋨ᛚ⹺ᐕ䋩

↳⺧⠪䈱⹏ଔ䋨%䋩

⴫ 39 ᛚ⹺ክᩏߦ㑐ߔࠆࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ㧔2006㨪2008ᐕ㧕

ᛚ⹺ᐕ N ਛᄩ୯ ᐔဋ୯ SD ᦨዊ ᦨᄢ PMDA

2006 38 60.0 57.9 8.6 40 85

2007 45 60.0 61.4 10.2 20 80

2008 43 70.0 69.4 8.2 40 83

ว⸘ 126 63.3 63.1 10.2 20 85

↳⺧⠪

2006 37 70.0 66.8 10.6 45 85

2007 45 70.0 66.6 9.4 45 80

2008 42 70.0 70.5 12.2 20 90

ว⸘ 124 70.0 68.0 10.8 20 90 Ꮕ䋨PMDA-↳⺧⠪䋩

2006 37 -5.0 -8.6 11.1 -30 15

2007 45 -5.0 -5.3 12.5 -45 25

2008 42 0.0 -1.1 12.5 -30 35

ว⸘ 124 -5.0 -4.9 12.4 -45 35

࿑ 39 ክᩏㇱ೎ߩࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ㧔2008ᐕ㧕

0 10 20 30 40 50 60 70 80 90 100

Grades

New Drug 1 New Drug 2 New Drug 3 New Drug 4

Bio 1 Bio 2 Overall

ᣂ⮎╙৻ㇱ ᣂ⮎╙ੑㇱ ᣂ⮎╙ਃㇱ ᣂ⮎╙྾ㇱ

↢‛╙৻ㇱ ↢‛╙ੑㇱ PMDAో૕

PMDA䈱ὐᢙ

70.0 65.0

ਛᄩ୯ 75.0

70.0 70.0

70.0 67.5

ᵈ㧦ὐ✢ߪో૕ߩਛᄩ୯

70.0

⴫ 40 ክᩏㇱ೎ߩࡄࡈࠜ࡯ࡑࡦࠬ⹏ଔ㧔2008ᐕ㧕

ክᩏㇱ N ਛᄩ୯ ᐔဋ୯ SD ᦨዊ ᦨᄢ ᣂ⮎ክᩏ╙৻ㇱ 29 75.0 72.1 9.5 50 90 ᣂ⮎ክᩏ╙ੑㇱ 29 65.0 62.2 14.8 30 85 ᣂ⮎ክᩏ╙ਃㇱ 25 70.0 70.6 12.0 40 90 ᣂ⮎ክᩏ╙྾ㇱ 28 67.5 67.5 9.5 50 90

↢‛♽ክᩏ╙৻ㇱ 9 70.0 71.1 10.5 60 90

↢‛♽ክᩏ╙ੑㇱ 3 70.0 63.3 11.5 50 70

9┨ ߹ߣ߼

2000㨪2008ᐕߦ࿖ౝߢᛚ⹺ߐࠇߚᣂක⮎ຠࠍኻ⽎ߦޔ⥃ᐥ㐿⊒ᦼ㑆㧔ೋ࿁ᴦ㛎⸘↹ዯឭ಴ᣣ㨪ᛚ⹺↳

⺧ᣣ㧕ޔክᩏᦼ㑆㧔ᛚ⹺↳⺧ᣣ㨪ᛚ⹺ᣣ㧕ޔਔ⠪ࠍวࠊߖߚ㐿⊒ᦼ㑆㧔ೋ࿁ᴦ㛎⸘↹ዯឭ಴ᣣ㨪ᛚ⹺ᣣ㧕 ߩផ⒖߅ࠃ߮ߘߩ㐳ߐߣ㑐ଥߔࠆ࿃ሶࠍᬌ⸛ߒߚޕ⥃ᐥ㐿⊒ᦼ㑆ߪ2000㨪2008ᐕߩਛᄩ୯߇59.5ࡨ᦬

㧔5.0ᐕ㧕ޔ2008ᐕ߇44.6ࡨ᦬㧔3.7ᐕ㧕ߢ޽ࠅޔ㐿⊒ᚢ⇛ߩᄙ᭽ൻࠍ෻ᤋߒߡߘߩᄌേ߿߫ࠄߟ߈ߪᄢ ߈߆ߞߚޕᄖ࿖Phase 2㨪3⹜㛎ᚑ❣ࠍ࿖ౝᛚ⹺↳⺧ߩᩮ᜚⾗ᢱߣߒߡ೑↪ߔࠆߎߣ߇৻⥸ൻߒߡ߈ߡ߅ ࠅޔNMEߢߪᄖ࿖⥃ᐥ࠺࡯࠲ࠍ೑↪ߒߚຠ⋡ߩ⥃ᐥ㐿⊒ᦼ㑆ߪ᦭ᗧߦ⍴߆ߞߚޕ2008ᐕߦᛚ⹺ߐࠇߚ 78ຠ⋡ߩ߁ߜޔ࿖㓙౒หᴦ㛎ߩᚑ❣ࠍ⹏ଔ⾗ᢱߣߒߚߩߪ1ຠ⋡ߩߺߢ޽ߞߚ߇ޔ࿖㓙౒หᴦ㛎ߦ㑐ߔ ࠆኻ㕙ഥ⸒߿ᴦ㛎⸘↹ዯ߇ᦨㄭჇടߒߡ޿ࠆߎߣ߆ࠄޔ⥃ᐥ࠺࡯࠲ࠍ࿖㓙⊛ߦ⋧੕೑↪ߔࠆ㐿⊒߇੹ᓟ Ⴧ߃ߡ޿ߊߣ੍ᗐߐࠇࠆޕ࿖㓙౒หᴦ㛎ߦࠃߞߡ⥃ᐥ㐿⊒ᦼ㑆߇⍴ߊߥࠆߩ߆ޔⶄᢙ࿖ߢታᣉߔࠆߎߣ

╬ߦࠃߞߡ㐳ߊߥࠆߩ߆ޔ޽ࠆ޿ߪᄢ߈ߊᄌࠊࠄߥ޿ߩ߆ߪ߹ߛਇ᣿ߢ޽ࠅޔ࿖ౝᄖߦ߅ߌࠆ⥃ᐥ㐿⊒

ߩ⌕ᚻᤨᦼ߿↳⺧ᤨᦼ߳ߩᓇ㗀߽฽߼ߡޔ੹ᓟᬌ⸛߇ᔅⷐߢ޽ࠆޕ

ክᩏᦼ㑆ߪ2004ᐕ4᦬ߩPMDA⸳┙ᓟ⍴❗௑ะߦ޽ࠅޔ9ᐕ㑆ࠍㅢߒߚਛᄩ୯ߪ20.6ࡨ᦬㧔1.7ᐕ㧕ޔ 2008ᐕߪ19.0ࡨ᦬㧔1.6ᐕ㧕ߢ޽ߞߚޕ↳⺧⠪ߪክᩏᦼ㑆߇ㄭᐕ⍴ߊߥߞߡ޿ࠆߎߣࠍ⹺⼂ߒߡ߅ࠅޔ PMDAߦኻߔࠆ⹏ଔ߽ᐕޘะ਄ߒߡ޿ࠆ߇ޔೋ࿁㕙⺣ᓟᾖળ੐㗄ߩ࿁╵ឭ಴߆ࠄㅊടᾖળ੐㗄ࠍ⚻ߡኾ 㐷ද⼏ߦ⥋ࠆࡊࡠ࠮ࠬߦᄙߊߩᤨ㑆ࠍⷐߒߡ߅ࠅޔ2008ᐕߩታ❣ߣޟ㕟ᣂ⊛ක⮎ຠ࡮ක≮ᯏེഃ಴ߩߚ

߼ߩ5ࡨᐕᚢ⇛ޠࠍฃߌߡឝߍߚ2011ᐕᐲߩ⋡ᮡ୯ߣߩ㑆ߦߪଐὼߣߒߡᄢ߈ߥᏅ߇ሽ࿷ߔࠆޕ ⴕ᡽ޔ↳⺧⠪෺ᣇߩᜬߜᤨ㑆ࠍߐࠄߦ⍴❗ߔࠆߚ߼ߦߪޔㅴⴕਛߩPMDA⡯ຬߩჇຬޔ੐೨⹏ଔ⋧⺣

೙ᐲߩዉ౉ࠍ฽߻ᴦ㛎⋧⺣ߩ᜛లޔክᩏߩㅴ᝞▤ℂߩᒝൻߣ޿ߞߚᣉ╷ࠍታലᕈߩ޽ࠆᒻߢታ⃻ߔࠆߎ ߣ߇㊀ⷐߢ޽ࠆޕ߹ߚޔ↳⺧⠪߽ᴦ㛎⋧⺣߿ᄖ࿖⥃ᐥ࠺࡯࠲ߩലᨐ⊛ߥᵴ↪ޔ⾰ߩ㜞޿↳⺧⾗ᢱߩឭ಴ޔ ᾖળ੐㗄ߦኻߔࠆㄦㅦߥ࿁╵ឭ಴╬ࠍታⴕߔࠆߣߣ߽ߦޔ୘ޘߩડᬺౝߩᚻ㗅߿૕೙ߩ⷗⋥ߒࠍ⠨ᘦߔ ࠆᔅⷐ߇޽ࠆߣ⠨߃ࠄࠇࠆޕPMDA⡯ຬߩჇടߦ㑐ߒߡߪޔߘߩലᨐߦᦼᓙߔࠆߣߣ߽ߦޔᧂ⚻㛎⠪ߩ ᕆჇ߿⚵❱ߩᄌᦝߦࠃߞߡPMDAߩታ❣߿⹏ଔ߇ࡑࠗ࠽ࠬߦォߓߥ޿ࠃ߁චಽߥੱ᧚⢒ᚑߣㆡಾߥੱ

ຬ㈩⟎߇ታᣉߐࠇࠆߎߣࠍ㗿߁ޕ

2009ᐕᐲࠃࠅ⹜㛎⊛ߦዉ౉ߐࠇߚ੐೨⹏ଔ⋧⺣೙ᐲߦ㑐ߒߡߪޔᛚ⹺↳⺧೨ߦឭ಴น⢻ߥຠ⾰ޔ㕖⥃

ᐥޔ⥃ᐥ࠺࡯࠲ࠍᴦ㛎⋧⺣ߩᨒ⚵ߺߩਛߢ⹏ଔߒޔ໧㗴ὐ߿⺖㗴ࠍ޽ࠄ߆ߓ߼․ቯߔࠆߎߣߦࠃߞߡክ ᩏߩല₸ൻߣᦼ㑆⍴❗ࠍ࿑ࠅޔክᩏࠍታ⾰⊛ߦ೨ୟߒߔࠆߎߣࠍ⋡⊛ߣߒߡ޿ࠆߣ޿߃ࠆޕ੐೨⹏ଔ⋧

⺣೙ᐲߩᚑᨐ߇ᛚ⹺ຠ⋡ߩክᩏᦼ㑆ߦ෻ᤋߐࠇࠆߩߪ2010ᐕએ㒠ߦߥࠆߣ੍ᗐߐࠇࠆ߇ޔᧄ೙ᐲ߇7.2.1 㗄ߢᬌ⸛ߒߚ↳⺧೨⋧⺣ߩࠃ߁ߦክᩏᦼ㑆߇⍴ߊߥࠆಽޔ⥃ᐥ㐿⊒ᦼ㑆߇ᑧ߮ࠆߎߣߥߊޔክᩏᦼ㑆߅ ࠃ߮㐿⊒ᦼ㑆ో૕ࠍ᦭ᗧߦ⍴❗ߒޔઁߩຠ⋡ߩክᩏࠍᅹߍࠆߎߣ߇ߥ޿ᒻߢታⴕߐࠇࠆߎߣࠍᦼᓙߔࠆޕ

߹ߚޔ੐೨⹏ଔ⋧⺣ࠍ೑↪ߒߚຠ⋡ߪ೑↪ߒߥ߆ߞߚຠ⋡ࠃࠅㄦㅦߦክᩏߐࠇࠆߎߣࠍ଻⸽ߔࠆ઀⚵ߺ ߇᭴▽ߐࠇޔㅊട⾌↪ࠍ⽶ᜂߔࠆ↳⺧⠪ߦߘߩࡌࡀࡈࠖ࠶࠻߇᣿⏕ߦ␜ߐࠇࠆᔅⷐ߽޽ࠆޕߐࠄߦޔክ ᩏㇱޔክᩏಽ㊁ޔᜂᒰ⠪㑆ߢ߫ࠄߟ߈ߩ޽ࠆክᩏࡊࡠ࠮ࠬߩᐔḰൻ߿ޔክᩏߩ⷗ㅢߒߩะ਄ߦߟߥ߇ࠆ ታലᕈߩ޽ࠆᮡḰ⊛ߥክᩏ࠲ࠗࡓ࡜ࠗࡦߩ᣿␜ޔᾖળ੐㗄ߩല₸ൻޔ⮎੐࡮㘩ຠⴡ↢ክ⼏ળߩක⮎ຠㇱ ળ߅ࠃ߮⮎੐ಽ⑼ળߩ৻ᧄൻ޽ࠆ޿ߪ㐿௅㗫ᐲߩ⷗⋥ߒߣ޿ߞߚὐ߽ᬌ⸛ߦ୯ߔࠆߣ⠨߃ࠄࠇࠆޕ

⃻࿷ޔડᬺ㑆ߥࠄ߮ߦPMDAߣડᬺߩ㑆ߢޔᛚ⹺↳⺧߅ࠃ߮ክᩏߩല₸ൻߦะߌߚ੐଀ߩ౒᦭߿ද⼏

߇ㅴࠎߢ޿ࠆޕᣂ⮎߳ߩࠕࠢ࠮ࠬะ਄ߦะߌޔ੹ᓟ߽ⴕ᡽ߣ↳⺧⠪߇ቯᦼ⊛ߥታ❣⹏ଔ߿ᗧ⷗੤឵ࠍㅢ ߓߡ෺ᣇߩᬺോࠍᡷༀߒޔߘߩᚑᨐ߇⥃ᐥ㐿⊒ᦼ㑆ߣክᩏᦼ㑆ࠍวࠊߖߚ㐿⊒ᦼ㑆ߩ⍴❗ߣߒߡ⃻ࠇࠆ ߎߣࠍᦼᓙߔࠆޕ

10┨ ᛚ⹺ክᩏ೙ᐲߦኻߔࠆ↳⺧ડᬺߩᗧ⷗ޔⷐᦸ

ᛚ⹺ክᩏ೙ᐲߦኻߔࠆ↳⺧ડᬺߩᗧ⷗߿ⷐᦸࠍᢙ୯ߢ⴫ߔߎߣߪ࿎㔍ߢ޽ࠆߚ߼ޔᛚ⹺ຠ⋡ߦ㑐ߔࠆ

⺞ᩏ␿Iߣߪ೎ߦޔ⺞ᩏ␿IIߦߡ2008ᐕߩᛚ⹺ຠ⋡ߩ↳⺧ડᬺ㧔౒ห㐿⊒ડᬺࠍ฽߻㧕ߦએਅߩ4ὐ ߦߟ޿ߡ࿁╵ࠍଐ㗬ߒߚޕ࿁╵ߪޔ↪⺆߿ᢥ૕ࠍᢛ஻ߒߚઁߪޔ࿁╵ડᬺ߿ຠ⋡╬߇․ቯߐࠇߥ޿▸࿐

ߢේᢥߩ߹߹ߣߒߚޕ

1. PMDA⸳┙એ㒠ߩ⚵❱࡮ᯏ⢻ߦ㑐ߔࠆⷐᦸޔᡷༀὐ

2. ክᩏㆃᑧߦ㑐ߔࠆⷐᦸޔክᩏㆊ⒟ߢߩ໧㗴੐଀

3. ੐೨⹏ଔ⋧⺣೙ᐲዉ౉ߦ㑐ߔࠆⷐᦸޔᗧ⷗

4. PMDAክᩏຬߩჇຬߦኻߔࠆᦼᓙޔ ᔨ

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